Gene therapySomatic–cell therapytertiary care hospitalATMPs
…nes for human use and are classified into three main categories:Gene therapy: uses recombinant genes created in the laboratory to treat, pre…
7articles mentioning treatments
11treatment mentions
1distinct treatments extracted
0%of mentions human-reviewed
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gene therapy
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Articles mentioning gene therapy
7 articles · page 1 of 1gene therapymuscular dystrophysickle cell diseasecystic fibrosishaemophiliaHIVreni-celrenizgamglogene autogedtemcelN Engl J Medhaemoglobinopathies
…atched donors, which has been the only option. Franco describes gene therapy as the attractive option, particularly for those without a matc…
gene therapyrare conditions
…The psychosocial impact of taking part in clinical trials of gene therapy for rare conditions on participants and their families is not w…
gene therapycochlear implantsaudiologyophthalmology
…Sensory restoration procedures, such as gene therapy in ophthalmology and cochlear implants in audiology, have the p…
gene therapyanticoagulationtransfusionshydroxyureasickle cell disease
…ding the role of hydroxyurea, transfusions, anticoagulation and gene therapy. By integrating multimodality imaging, updated guideline recomm…
gene therapyenzyme replacement therapystem cell therapysingle-gene disorders
…Background Recent advances in gene therapy, stem cell therapy, and enzyme replacement therapy offer early …
substrate substitutiongene therapyGNE myopathydistal myopathynhs.net
…or promising treatment in preclinical and clinical studies from substrate substitution to gene therapy options. Therefore, the increasing recognition …