adeno-associated virus-based gene replacement therapynusinersenonasemnogene abeparvovecspinal muscular atrophynewborn screening
…ersen before consideration of onasemnogene abeparvovec (OA), an adeno-associated virus-based gene replacement therapy.…
1articles mentioning treatments
1treatment mentions
1distinct treatments extracted
0%of mentions human-reviewed
adeno-associated virus-based gene replacement therapy
This treatment is selected. Its supporting articles are shown below.