small interfering RNA treatmentsGalNAc conjugationhereditary transthyretin amyloidosisgenetic liver diseasesrare diseasesnon-human primatesLipid nanoparticle-mRNA therapeuticsRNA-based therapeutics
…ress in the treatment of genetic liver diseases, exemplified by small interfering RNA treatments for hereditary transthyretin amyloidosis, which use liver-targe…