luspatercepthydroxyurea (HU)β-thalassemia major (BTM)University of Karachiiron chelationSaint judes hospitalChildren’s Hospital KarachiThe Children hospitalβ-thalassemiaemerging gene therapies+1 more
…ed. 2018;378:1479–1493.Cappellini MD, et al. A phase 3 trial of luspatercept in patients with transfusiondependent β- thalassemia. N. Engl. …