TofersenMNDSt George’s Hospital
…howed pathogenic mutations and three patients were treated with Tofersen. 29% of those offered testing did not proceed to test activatio…
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…howed pathogenic mutations and three patients were treated with Tofersen. 29% of those offered testing did not proceed to test activatio…
… mutations opens the door to disease-modifying therapies (e.g., Tofersen for SOD1), which have the potential to alter disease progressio…