Lipid nanoparticle-mRNA therapeuticsRNA-based therapeuticshereditary transthyretin amyloidosisgenetic liver diseasesrare diseasesnon-human primatessmall interfering RNA treatmentsGalNAc conjugation
…ng delivery methods and ensuring long-term safety and efficacy. Lipid nanoparticle-mRNA therapeutics, particularly for protein replacement in rare diseases, have ga…