Eladocagene exuparvovecEL-EXEL-EXOculogyric crisesAromatic L-amino acid decarboxylase deficiencyAADC deficiency
…severe motor impairment, oculogyric crises and high care needs. Eladocagene exuparvovec (EL-EX) is an intracerebral AAV2 gene therapy for patients ≥18 …