rare conditionsgene therapy
…al impact of taking part in clinical trials of gene therapy for rare conditions on participants and their families is not well understood. Syst…
2articles mentioning diseases
2disease mentions
1distinct diseases extracted
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rare conditions
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Articles mentioning rare conditions
2 articles · page 1 of 1rare conditionstherapeutic agent
…ical advances are to be realised. This is none more so than for rare conditions—for which there may be no available treatments and where the sm…