Friedreich ataxiaFrataxin
…ings support advancing its candidacy as a surrogate endpoint in Friedreich ataxia.…
Entity family
Named diseases, disorders, syndromes, injuries, and health conditions. Examples include epilepsy, diabetes, stroke.
This disease is selected. Its supporting articles are shown below.
…ings support advancing its candidacy as a surrogate endpoint in Friedreich ataxia.…
…Friedreich ataxia (FRDA) is a progressive neurodegenerative disorder with limited…