93.1%
ATTRv amyloidosisCNS/leptomeningeal amyloidosisGly53Ala ATTRv amyloidosisCNS amyloidosistafamidistolcaponepatisiran
…ggregate inhibitor. Treatment options for CNS manifestations of ATTRv amyloidosis requires further research.References Monteiro Cecilia, et al. C…